Bookedited by Theodore Friedman.
Contents:
General principles of retrovirus vector design / Tammy Chang and Jiing-Kuan Yee
Strategies for retrovirus-based correction of severe, combined immunodeficiency (SCID) / Alain Fischer, Salima Hacein-Bey-Abina, and Marina Cavazzana-Calvo
Retrovirus and lentivirus vector design and methods of cell conditioning / Samantha Cooray, Steven J. Howe, and Adrian J. Thrasher
Analysis of the clonal repertoire of gene-corrected cells in gene therapy / Anna Paruzynski ... [et al.]
Developing novel lentiviral vectors into clinical products / Anna Leath and Kenneth Cornetta
Lentivirus vectors in [beta]-thalassemia / Emmanuel Payen ... [et al.]
Gene therapy for chronic granulomatous disease / Elizabeth M. Kang and Harry L. Malech
Alternative splicing caused by lentiviral integration in the human genome / Arianna Moiani and Fulvio Mavilio
Genotoxicity assay for gene therapy vectors in tumor prone mice / Eugenio Montini and Daniela Cesana
Lentiviral hematopoietic cell gene therapy for X-linked adrenoleukodystrophy / Nathalie Cartier ... [et al.]
Retroviral replicating vectors in cancer / Christopher R. Logg ... [et al.]
Adeno-associated virus vectorology, manufacturing, and clinical applications / Joshua C. Grieger and R. Jude Samulski
Gene delivery to the retina : from mouse to man / Jean Bennett, Daniel C. Chung, and Albert Maguire
Generation of hairpin-based RNAi vectors for biological and therapeutic application / Ryan L. Boudreau and Beverly L. Davidson
Recombinant adeno-associated viral vector reference standards / Philippe Moullier and Richard O. Snyder
NIH oversight of human gene transfer research involving retroviral, lentiviral, and adeno-associated virus vectors and the role of the NIH Recombinant DNA Advisory Committee / Marina O'Reilly ... [et al.]
Regulatory structures for gene therapy medicinal products in the European Union / Bettina Klug ... [et al.].